Rare diseases have a devastating impact on people’s lives: pharmaceutical companies here in the UK and around the world are working to change that – developing new medicines to give families hope for the future.
The UK government and devolved administrations published the UK Rare Diseases Framework in January 2021, setting out a shared vision for addressing health inequalities and improving the lives of people living with rare diseases across the UK.
The framework outlined 4 key national priorities:
- helping patients get a final diagnosis faster
- increasing awareness among healthcare professionals
- better co-ordination of care
- improving access to specialist care, treatment and drugs
To turn this vision into action, each of the 4 UK nations developed nation-specific action plans detailing how these priorities will be addressed.
We’re facing three challenges:
Last modified: 22 March 2022
Last reviewed: 1 August 2022